How to do gene therapy

Gene therapy requires some way of delivering a functioning gene into the cells of a patient. In recent trials, several different ways have been researched, using carriers to deliver the gene.

  • Disabled viruses can transfer genes into a cell efficiently. However, it can be difficult to make a virus totally harmless so some disease symptoms associated with the virus may also develop.
  • Non-viral carriers include fat globules called liposomes and artificial chromosomes, where a sequence of DNA is created in a laboratory. These can transport large amounts of DNA, but they are not as easily incorporated into the genetic material of the cell.

Try cutting out a gene of interest - interactive